Molecular Therapy
Volume 27, Issue 7, 3 July 2019, Pages 1215-1227
Original ArticleTargeting a Pre-existing Anti-transgene T Cell Response for Effective Gene Therapy of MPS-I in the Mouse Model of the Disease
Under a Creative Commons license
open access
Keywords
gene therapy
MPS-I
ERT
immune response
pre-existing immunity
lentiviral vector
HSC
depleting agents
fludarabine
Cited by (0)
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These authors contributed equally to this work.
© 2019 The Authors.