Molecular Therapy
Volume 10, Issue 3, September 2004, Pages 478-491
ArticleWidespread Correction of Lysosomal Storage Following Intrahepatic Injection of a Recombinant Adeno-associated Virus in the Adult MPS VII Mouse
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Keywords
gene therapy
gene transfer techniques
adeno-associated virus
lysosomal storage diseases
mucopolysaccharidosis VII
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Copyright © 2004 The American Society of Gene Therapy. Published by Elsevier Inc. All rights reserved.